LATEST ARTICLES
Advances on many fronts in the battle against the protein that...
This fall sees exciting announcements from a number of companies focused on novel Huntingtin Lowering technologies, including Wave, PTC and Voyager
We’ve had a run...
Voyager Therapeutics Announces Preclinical Data for Huntington’s Disease and Amyotrophic Lateral...
One-time delivery of VY-HTT01 for Huntington’s disease achieves significant reduction of HTT gene expression in deeper tissues and outer layers of the brain of...
HDSA FAQ on the Roche/Genentech RG6042 program
HDSA's frequently asked questions factsheet about the huntingtin-lowering trial ASO program was so good we stole it (with permission)
n Wednesday, September 26th, HDSA hosted...
UNIVERSITY
USC scientists map brain region linked to Alzheimer’s and other diseases
Researchers show structures, nerve connections and functions in vivid detail as part of the most detailed atlas yet of a person’s memory bank
USC scientists...
Study Suggests Potential Therapy for Huntington’s Disease
A new study published in the Proceedings of the National Academy of Sciences (PNAS) suggests that Huntington’s disease may take effect much earlier in life than...
New insight into Huntington’s disease may open door to drug development
Researchers have developed a new theory on Huntington’s disease which is being welcomed for showing promise to open new avenues of drug development for...
Scientists develop new approach to understand Huntington’s
Neurological diseases are typically associated with a multitude of molecular changes. But out of these thousands of changes in gene expression, which ones are...
HDBUZZ
HDSA FAQ on the Roche/Genentech RG6042 program
HDSA's frequently asked questions factsheet about the huntingtin-lowering trial ASO program was so good we stole it (with permission)
n Wednesday, September 26th, HDSA hosted...
Roche announces details of its ‘pivotal’ huntingtin-lowering study
The GENERATION-HD1 trial will test whether RG6042 – formerly Ionis-HTTRx – slows the progression of Huntington's disease
t’s a time of huge developments in the...
ARTICLES
IONIS-HTTRx
