LATEST ARTICLES
Novartis receives US Food and Drug Administration (FDA) Orphan Drug Designation...
Novartis today announced that the US Food and Drug Administration (FDA) has granted Orphan Drug Designation for branaplam (LMI070) in Huntington’s disease (HD). An...
uniQure Announces Enrollment of Next Two Patients in Phase I/II Clinical...
uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs, today announced that two additional patient procedures...
Updates from the EHDN Plenary Meeting 2020
Read our summary of the latest updates from the EHDN Plenary Meeting 2020
In September, the European Huntington’s Disease Network (EHDN) hosted a virtual webinar...
UNIVERSITY
World first study reveals altered gut bacteria in Huntington’s Disease which...
The first clinical study of the gut microbiome in Huntington’s disease (HD) has found evidence of gut dysbiosis (altered bacteria in the gastrointestinal tract) in people...
Neural vulnerability in Huntington’s disease tied to release of mitochondrial RNA
In the first study to comprehensively track how different types of brain cells respond to the mutation that causes Huntington’s disease (HD), MIT neuroscientists...
Study reveals intricate details about Huntington’s disease protein
The research adds to a body of work devoted to understanding the protein’s role in cell biology and health
A new study reveals intricate details...
Ohio State Conducts First Gene Therapy Clinical Trial For Huntington’s Disease
COLUMBUS, Ohio – In a worldwide first, surgeons at The Ohio State University Wexner Medical Center have treated two patients with Huntington’s disease using a novel...
HDBUZZ
Updates from the EHDN Plenary Meeting 2020
Read our summary of the latest updates from the EHDN Plenary Meeting 2020
In September, the European Huntington’s Disease Network (EHDN) hosted a virtual webinar...
When genes are unstable: targeting somatic instability in HD
CAG repeats expand in some parts of the body and brain as people with HD get older, a phenomenon known as somatic instability. Learn...
ARTICLES
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