LATEST ARTICLES

8th Plenary Meeting EHDN 2014 Barcelona: 19-21 settembre 2014 – Report

Annarita Bentivoglio* - Marina Frontali** Si è appena concluso l’ottavo meeting plenario del Network Europeo per la Malattia di Huntington. Oltre 900 partecipanti: l’incontro più numeroso che sia stato mai organizzato sulla Malattia di Huntington. Un...

Fatal cellular malfunction identified in Huntington’s disease

Researchers believe they have learned how mutations in the gene that causes Huntington’s disease kill brain cells, a finding that could open new opportunities for treating the fatal disorder. Scientists first linked the gene...

Details emerge of first Huntington’s disease gene therapy clinical trial

UniQure announces key details of its planned trial to assess the safety and ability of AMT-130 gene therapy to lower the problematic huntingtin protein using a ‘single-shot’ virus delivery system. At the recent Huntington’s Disease...

EIP Pharma Initiates New Study with Neflamapimod for the Treatment of Cognitive Deficits in...

EIP Pharma, Inc., a CNS-focused therapeutics company, today announced the initiation of a new Phase 2 proof-of-concept study evaluating neflamapimod as a treatment for the cognitive dysfunction associated with Huntington's disease, a rare, genetically inherited disease...

Sangamo Therapeutics Announces Nature Medicine Publication Detailing the Activity of Disease Allele-Selective Zinc Finger...

Jul. 1, 2019-- Sangamo Therapeutics, Inc. (Nasdaq: SGMO), a genomic medicine company, today announced the publication of a manuscript describing the activity of allele-selective zinc finger protein transcription-factors (ZFP-TFs) in preclinical models of Huntington’s disease (HD)....

Distinct clinical profiles of Huntington’s disease can be associated with two specific neural signatures

Cognitive-motor and psychiatric profiles of Huntington's disease show a different pattern of brain alterations The identification of specific neural signatures can help develop specific biomarkers and personalized treatments for Huntington's disease. •    Research results underscore the...

BGU Scientists Duplicate Blood-Brain Barrier Outside the Body

​Scientists can't make a living copy of your brain outside your body. That's the stuff of science fiction. But in a new study, they duplicated a critical brain structure, the blood-brain barrier (BBB) that...